In a groundbreaking medical achievement, an infant from Pennsylvania, referred to as KJ, has become the first person to ...

A US baby born with a rare and life-threatening genetic disease is thriving after undergoing the first successful ...

A research team has developed and safely delivered a personalized gene editing therapy to treat an infant with a life-threatening, incurable genetic disease. The infant, who was diagnosed with the ...

In a groundbreaking medical milestone, U.S. researchers have successfully developed and delivered a personalized ...

The one-off treatment highlights the promise of a new type of gene editing and the challenges of using it to treat extremely ...

An infant with a rare urea cycle disorder became the first patient to receive a personalized gene-editing therapy. His care ...

Gene therapy has always held enormous promise to correct genetic diseases, but turning that potential into treatments has ...

A baby known as KJ is the first person in the world to receive a customized CRISPR therapy designed to fix a specific ...

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a ...

In a world first, scientists used CRISPR to fix a baby's unique genetic mutation. The report offers hope for personalized ...